Professor Patrick Yu Wai Man has outlined how mitochondrial biology, clinical genetics and ocular gene therapy have started ...

Cell and gene therapies are moving towards correcting root causes of diseases. Let's take a look at future cell and gene therapy trends.

Dr Romain Joubert of AviadoBio explained how the company has used an adeno-associated virus gene replacement programme in ...

UF scientist develops safer gene therapy restoring vision in children with rare inherited eye diseases; pivotal trials begin ...

Forbes contributors publish independent expert analyses and insights. A patient in a late-stage gene editing trial for a rare heart condition died from fatal liver complications after receiving an ...

2025 was a rollercoaster year for the cell and gene therapy field. Stories such as the successful treatment of ‘Baby KJ’ using a bespoke gene editor developed through a public–private partnership, and ...

Life Biosciences is pushing cellular rejuvenation into the clinic with ER-100, an experimental gene therapy designed to restore vision by reviving damaged neurons in the eye. Rather than slowing ...

The rapid evolution of CRISPR/Cas genome editing has redefined the possibilities of cellular and gene therapy, enabling precise correction, ...

The idea behind intra-articular gene therapy for treating osteoarthritis (OA) is to deliver the gene-altering vector or cells directly to the precise site of the disease with a single injection — so ...

A new software package called CREsted, published in Nature Methods, gives researchers an end-to-end workflow for modeling and ...